Tag: sickle

The revolutionary sickle cell therapies

Editor’s Note: Elizabeth Yuko, Ph.D., is a bioethicist and writer whose work has appeared in The New York Times, Rolling Stone, The Washington Post, The Atlantic and elsewhere. She is also an adjunct professor at Fordham University. The views expressed here are hers. Read more opinion on CNN. In December, the US Food and Drug Administration (FDA) approved the first […]

US regulators approve two gene therapies for sickle cell disease | US news

The US Food and Drug Administration has approved a pair of gene therapies for sickle cell disease, including the first treatment based on the breakthrough Crispr gene-editing technology, opening up two “transformative therapy” avenues for some patients. The FDA approved Lyfgenia from Bluebird Bio, and a separate treatment called Casgevy by partners Vertex Pharmaceuticals and […]