Tag: gene

Takeaways from AP’s report on access to gene therapies for rare diseases

The promise of gene therapy looms large for families dealing with rare, genetic disorders. Such treatments offer the possibility of one-time cures. But families and researchers worry such therapies will remain out of reach. Collectively, about 350 million people worldwide suffer from rare diseases, most of which are genetic. But each of the 7,000 individual […]

AI plus gene editing promises to shift biotech into high gear

During her chemistry Nobel Prize lecture in 2018, Frances Arnold said, “Today we can for all practical purposes read, write and edit any sequence of DNA, but we cannot compose it.” That isn’t true anymore. Since then, science and technology have progressed so much that artificial intelligence has learned to compose DNA, and with genetically […]

UK toddler regains hearing in gene therapy breakthrough

STORY: Banging on blocks and playing the flute, Opal Sandy looks like an average energetic toddler. :: May 1, 2024 It would be hard to tell she was born deaf – and unable to hear just months earlier. :: Oxfordshire, England She’s the first patient in England to regain her hearing through gene therapy. :: […]