You generally hear one of two contradictory narratives about weight loss. The first is that your weight is simply the result of how much you eat and how much you exercise, but the second is that some people’s bodies pack on weight much more easily than others, making weight loss a much more difficult goal. […]
Tag: gene
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate
Robin Alderman faces an agonizing reality: Gene therapy might cure her son Camden’s rare, inherited immune deficiency. But it’s not available to him. In 2022, London-based Orchard Therapeutics stopped investing in an experimental treatment for the condition, Wiskott-Aldrich syndrome. And there are no gene therapy studies he can join. “We feel like we are the […]
Takeaways from AP’s report on access to gene therapies for rare diseases
The promise of gene therapy looms large for families dealing with rare, genetic disorders. Such treatments offer the possibility of one-time cures. But families and researchers worry such therapies will remain out of reach. Collectively, about 350 million people worldwide suffer from rare diseases, most of which are genetic. But each of the 7,000 individual […]
AI plus gene editing promises to shift biotech into high gear
During her chemistry Nobel Prize lecture in 2018, Frances Arnold said, “Today we can for all practical purposes read, write and edit any sequence of DNA, but we cannot compose it.” That isn’t true anymore. Since then, science and technology have progressed so much that artificial intelligence has learned to compose DNA, and with genetically […]
Researchers find a single, surprising gene behind a disorder that causes intellectual disability
Scientists have found the genetic root of a disorder that causes intellectual disability, which they estimate affects as many as one in 20,000 young people. And they hope their discovery leads to a new diagnosis that can provide answers to families. Those with the condition have a constellation of issues, which also include short stature, […]
Four takeaways from UCLA Chancellor Gene Block’s testimony on campus antisemitism, protests
UCLA Chancellor Gene Block found himself in the nation’s culture wars hot seat Thursday, interrogated by members of Congress about his handling of complaints of campus antisemitism, amid student protests over the Israel-Hamas war. For Republican Congress members, the hearing organized by the GOP-led House Committee on Education and the Workforce was a chance to […]
The stock market’s bull rally could last another 5 years, but it’ll end in a ‘spectacular bursting of a bubble,’ veteran tech investor Gene Munster says
There’s a 3-5 year bull market forming in tech stocks, according to Gene MunsterBrian Ach/Getty Images The stock market’s current bull rally could last for another 5 years, according to tech analyst Gene Munster. Munster said a new crop of AI companies will go public and drive a boom in the stock market. But Munster […]
UK toddler regains hearing in gene therapy breakthrough
STORY: Banging on blocks and playing the flute, Opal Sandy looks like an average energetic toddler. :: May 1, 2024 It would be hard to tell she was born deaf – and unable to hear just months earlier. :: Oxfordshire, England She’s the first patient in England to regain her hearing through gene therapy. :: […]
People with two copies of a risk gene have genetic form of Alzheimer’s, scientists say
By Julie Steenhuysen CHICAGO (Reuters) -People who carry two copies of the APOE4 gene are virtually guaranteed to develop Alzheimer’s and face symptoms at an earlier age, researchers reported on Monday in a study that could redefine such carriers as having a new genetic form of the mind-wasting disease. The reclassification could change Alzheimer’s research, […]
A subset of Alzheimer’s cases may be caused by two copies of a single gene, new research shows
WASHINGTON (AP) — For the first time, researchers have identified a genetic form of late-in-life Alzheimer’s disease — in people who inherit two copies of a worrisome gene. Scientists have long known a gene called APOE4 is one of many things that can increase people’s risk for Alzheimer’s, including simply getting older. The vast majority […]
Experimental gene therapy restores some vision in patients with inherited blindness
For her entire life, college student Olivia Cook had only a small degree of central vision. It was as if she was watching the world through a straw hole, and in dimly lit places, she could not make out people’s faces, only their silhouettes. But after receiving an experimental gene-editing treatment to one of her […]